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Stem cell gene therapy could be key to treating Duchenne muscular dystrophy


February 11, 2016

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Scientists at the University of California, Los Angeles, have developed a new approach that could eventually be used to treat Duchenne muscular dystrophy. The stem cell gene therapy could be applicable for 60 percent of people with Duchenne, which affects approximately 1 in 5,000 boys in the U.S. and is the most common fatal childhood genetic disease.Full Story

Source
University of California, Los Angeles, Health Sciences

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